Buscar resultados de ensayos clínicos
Distal Myopathies - 12 Studies Found
Estado | Estudiar |
Active, not recruiting |
Nombre del estudio: Phase 3 Randomized, Double-Blind, Placebo-Controlled Study to Evaluate Sialic Acid in Patients With GNE Myopathy (GNEM) or Hereditary Inclusion Body Myopathy (HIBM) Condición:
|
Completed |
Nombre del estudio: Pharmacokinetic Study on N-acetylneuraminic Acid Condición:
Fecha: 2010-11-08 Intervenciones: Drug: NPC-09 NPC-09 tablet NPC-09 contains 50mg or 100mg N-acetylneuraminic acid (anhydride) |
Enrolling by invitation |
Nombre del estudio: Study to Evaluate the Safety and Efficacy of Ace-ER Tablets in Patients With GNE Myopathy or Hereditary Inclusion Body Myopathy Condición:
|
Recruiting |
Nombre del estudio: GNE-Myopathy Disease Monitoring Program (GNEM-DMP): A Registry and Prospective Observational Natural History Study to Assess GNE Myopathy or Hereditary Inclusion Body Myopathy (HIBM) Condición:
|
Recruiting |
Nombre del estudio: A Study to Evaluate the Safety of Aceneuramic Acid Extended Release (Ace-ER) Tablets in GNE Myopathy (GNEM) (Also Known as Hereditary Inclusion Body Myopathy (HIBM)) Patients With Severe Ambulatory Impairment Condición:
|
Completed |
Nombre del estudio: A Phase 2 Study to Evaluate the Dose and Pharmacodynamic Efficacy of Sialic Acid-Extended Release (SA-ER) Tablets in Patients With GNE Myopathy or Hereditary Inclusion Body Myopathy Condición:
Fecha: 2012-01-17 Intervenciones:
|
Completed |
Nombre del estudio: Phase I Clinical Trial of ManNAc in Patients With GNE Myopathy or Hereditary Inclusion Body Myopathy (HIBM) Condición:
Fecha: 2012-07-03 Intervenciones: Drug: ManNAc Single dose |
Recruiting |
Nombre del estudio: A Natural History Study of Patients With GNE Myopathy Condición: Hereditary Inclusion Body Myopathy Fecha: 2011-08-13 |
Completed |
Nombre del estudio: Safety and Pharmacokinetics of Sialic Acid Tables in Patients With Hereditary Inclusion Body Myopathy (HIBM) Condición: Hereditary Inclusion Body Myopathy (HIBM) Fecha: 2011-05-20 Intervenciones:
|
Completed |
Nombre del estudio: Intravenous Immune Globulin to Treat Hereditary Inclusion Body Myopathy Condición: Hereditary Inclusion Body Myopathy Fecha: 2005-09-18 Intervenciones: Drug: Immune Globulin |