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Medium-chain Acyl-coenzyme A Dehydrogenase Deficiency - 3 Studies Found
Estado | Estudiar |
Completed |
Nombre del estudio: Use of Ravicti™ in Patients With MCAD Deficiency With the 985A>G (K304E) Mutation Condición: Medium-chain Acyl-CoA Dehydrogenase (MCAD) Deficiency Fecha: 2013-06-13 Intervenciones: Drug: Ravicti Open-label design comparing Ravicti at doses of 2, 4, and 6 grams/m2/day |
Recruiting |
Nombre del estudio: Fatty Acid Oxidation Defects and Insulin Sensitivity Condición:
Intervenciones: |
Recruiting |
Nombre del estudio: Fat and Sugar Metabolism During Exercise in Patients With Metabolic Myopathy Condición:
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